Newcells provides a reliable and quick in vitro safety and efficacy service for evaluating novel compounds for retinal therapy with complex human retinal organoid or retinal pigment epithelium (RPE) ...

Cell and gene therapies are exciting new modalities that have the potential to treat, and even cure, a range of diseases that may not be possible with small molecules or monoclonal antibodies. However ...

Nanoparticle-mediated hyperthermia for cancer therapy is a growing area of cancer nanomedicine because of the potential for localized and targeted destruction of cancer cells. Localized hyperthermal ...

A UCLA-led team has developed a machine-learning model that can predict with a high degree of accuracy the short-term survival of dialysis patients on continuous renal replacement therapy (CRRT). The ...

The first peer-reviewed journal in the field of human gene therapy, providing all-inclusive coverage of the research, methods, and clinical developments that are driving today's explosion of gene ...

Spinal muscular atrophy (SMA) is a rare but serious neuromuscular disorder that causes worsening muscle weakness. SMA is a genetic, or inherited, disorder caused by a change in the SMN1 gene that ...

The spectrum of metabolic dysfunction-associated steatotic liver disease (MASLD) ranges from simple lipid accumulation in the human liver, to steatohepatitis with inflammation, fibrosis, cirrhosis, ...